In vivo adenine base editing rescues adrenoleukodystrophy in a humanized mouse model
已完结10由 妮妮 发布于 2024/10/11 11:44:40
DOI:10.1016/j.ymthe.2024.05.027
作者:Ramu Gopalappa, MinYoung Lee, Globinna Kim, Eul Sik Jung, Hanahrae Lee, Hye-Yeon Hwang, Jong Geol Lee, Su Jung Kim, Hyun Ju Yoo, Young Hoon Sung, Daesik Kim, In-Jeoung Baek, Hyongbum Henry Kim
文献类型:期刊论文
补充材料:只需要正文
文献链接:https://doi.org/10.1016/j.ymthe.2024.05.027